Pages that link to "Q36242842"
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The following pages link to Efficient photoreceptor-targeted gene expression in vivo by recombinant adeno-associated virus (Q36242842):
Displaying 50 items.
- A novel adeno-associated viral variant for efficient and selective intravitreal transduction of rat Müller cells (Q21142728) (← links)
- Lentiviral gene transfer of RPE65 rescues survival and function of cones in a mouse model of Leber congenital amaurosis (Q21144697) (← links)
- Production of high-titer recombinant adeno-associated virus vectors in the absence of helper adenovirus (Q24523073) (← links)
- Circular intermediates of recombinant adeno-associated virus have defined structural characteristics responsible for long-term episomal persistence in muscle tissue (Q24523651) (← links)
- Latent adeno-associated virus infection elicits humoral but not cell-mediated immune responses in a nonhuman primate model (Q24527302) (← links)
- Ectopic expression of a microbial-type rhodopsin restores visual responses in mice with photoreceptor degeneration (Q24547085) (← links)
- Structural and functional impairment of endocytic pathways by retinitis pigmentosa mutant rhodopsin-arrestin complexes (Q24563320) (← links)
- Lentiviral expression of retinal guanylate cyclase-1 (RetGC1) restores vision in an avian model of childhood blindness (Q27307727) (← links)
- Comparative analysis of DNA nanoparticles and AAVs for ocular gene delivery (Q27325842) (← links)
- Dosage thresholds for AAV2 and AAV8 photoreceptor gene therapy in monkey (Q27329160) (← links)
- MicroRNA-restricted transgene expression in the retina (Q27332143) (← links)
- Structural Insights into Adeno-Associated Virus Serotype 5 (Q27679454) (← links)
- Gene transfer mediated by recombinant baculovirus into mouse eye (Q28365551) (← links)
- Gene therapy prevents photoreceptor death and preserves retinal function in a Bardet-Biedl syndrome mouse model. (Q28507533) (← links)
- Potential long-term inhibition of ocular neovascularisation by recombinant adeno-associated virus-mediated secretion gene therapy (Q31065469) (← links)
- Adeno-associated virus type-2 expression of pigmented epithelium-derived factor or Kringles 1-3 of angiostatin reduce retinal neovascularization (Q31081886) (← links)
- Recombinant adeno-associated virus vector expressing angiostatin inhibits preretinal neovascularization in adult rats (Q31139438) (← links)
- Genetic fate of recombinant adeno-associated virus vector genomes in muscle (Q33186207) (← links)
- Long-term safety of GDNF gene delivery in the retina (Q33221962) (← links)
- Efficient non-viral ocular gene transfer with compacted DNA nanoparticles (Q33267297) (← links)
- XIAP protection of photoreceptors in animal models of retinitis pigmentosa (Q33279531) (← links)
- Designer gene delivery vectors: molecular engineering and evolution of adeno-associated viral vectors for enhanced gene transfer (Q33296224) (← links)
- Intraocular route of AAV2 vector administration defines humoral immune response and therapeutic potential (Q33374015) (← links)
- In vivo imaging of microscopic structures in the rat retina (Q33478311) (← links)
- Cloning and characterization of adeno-associated virus type 5. (Q33641228) (← links)
- The Gordon Wilson Lecture. From basic virology to human gene therapy. (Q33644983) (← links)
- Adeno-associated virus vectors and hematology (Q33695816) (← links)
- Adeno-associated viral vectors for gene transfer and gene therapy (Q33701559) (← links)
- Gene therapy in the treatment of ocular inflammation (Q33717725) (← links)
- Structure of adeno-associated virus type 4. (Q33724158) (← links)
- Self-complementary AAV5 vector facilitates quicker transgene expression in photoreceptor and retinal pigment epithelial cells of normal mouse. (Q33787600) (← links)
- An evolved adeno-associated viral variant enhances gene delivery and gene targeting in neural stem cells (Q33790771) (← links)
- Nonrandom transduction of recombinant adeno-associated virus vectors in mouse hepatocytes in vivo: cell cycling does not influence hepatocyte transduction (Q33802664) (← links)
- Design and packaging of adeno-associated virus gene targeting vectors (Q33804483) (← links)
- Structured illumination multimodal 3D-resolved quantitative phase and fluorescence sub-diffraction microscopy (Q33824570) (← links)
- AAV2-mediated subretinal gene transfer of hIFN-α attenuates experimental autoimmune uveoretinitis in mice (Q33911304) (← links)
- Recent advances in the molecular basis of inherited photoreceptor degeneration (Q33942183) (← links)
- Recombinant adenoassociated virus in cancer gene therapy (Q33970439) (← links)
- Ribozyme uses in retinal gene therapy. (Q34058780) (← links)
- Gene therapy and retinitis pigmentosa: advances and future challenges (Q34084443) (← links)
- Replacement gene therapy with a human RPGRIP1 sequence slows photoreceptor degeneration in a murine model of Leber congenital amaurosis (Q34085940) (← links)
- P2Y2Receptor Agonist INS37217 Enhances Functional Recovery after Detachment Caused by Subretinal Injection in Normal andrdsMice (Q34120951) (← links)
- Immune response following intraocular delivery of recombinant viral vectors (Q34198445) (← links)
- Adaptive optics retinal imaging in the living mouse eye (Q34264986) (← links)
- Virus-mediated transduction of murine retina with adeno-associated virus: effects of viral capsid and genome size. (Q34342913) (← links)
- Efficient gene transfer to retinal pigment epithelium cells with long-term expression (Q34406695) (← links)
- Gene targeting to the retina (Q34416392) (← links)
- Vector platforms for gene therapy of inherited retinopathies. (Q34561531) (← links)
- Gene therapy for retinal and choroidal diseases (Q34701404) (← links)
- Good manufacturing practice production of self-complementary serotype 8 adeno-associated viral vector for a hemophilia B clinical trial (Q34843808) (← links)